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  • Marina Caballero Bellón, Faura A, Margarit A, Bobillo-Perez S, Català-Temprano A, Alonso-Saladrigues A, Conde N, Balaguer-Gargallo M, Rives-Solà S and Jordán-García I.

    Outcomes for paediatric acute leukaemia patients admitted to the paediatric intensive care unit

    EUROPEAN JOURNAL OF PEDIATRICS . 181(3): 1037-1045. Nº de citas: 3

    [doi:10.1007/s00431-021-04292-9]

  • Ortiz-Maldonado V, Rives-Solà S, Español-Rego M, Alonso-Saladrigues A, Montoro M, Magnano L, Giné E, Pascal M, Díaz-Beyá M, Castella M, Català-Temprano A, Faura A, Rodríguez-Lobato LG, Oliver-Caldes A, Martínez-Roca A, Rovira M, González-Navarro EA, Ortega JR, Cid J, Lozano M, Garcia-Rey E, Fernández S, Castro P, Jordán-García I, Villamor N, Aymerich M, Torrebadell-Burriel M, Deyà-Martinez A, Fernández de Larrea C, Benitez-Ribas D, Trias E, Varea S, Calvo G, Esteve J, Urbano-Ispizua A, Juan-Otero M and Delgado J.

    Factors associated with the clinical outcome of patients with relapsed/refractory CD19+ acute lymphoblastic leukemia treated with ARI-0001 CART19-cell therapy

    Journal for ImmunoTherapy of Cancer . 9(12): 3644. Nº de citas: 9

    [doi:10.1136/jitc-2021-003644]

  • Mesegue-Meda M, Alonso-Saladrigues A, Pérez-Jaume S, Comes-Escoda A, Dapena JL, Faura A, Conde N, Català-Temprano A, Ruiz-Llobet A, Zapico-Muñiz E, Camós-Guijosa M and Rives-Solà S.

    Lower incidence of clinical allergy with PEG-asparaginase upfront versus the sequential use of native E. coli asparaginase followed by PEG-ASP in pediatric patients with acute lymphoblastic leukemia.

    HEMATOLOGICAL ONCOLOGY . 39(5): 687-696. Nº de citas: 4

    [doi:10.1002/hon.2914]

  • Sahoo SS, Pastor VB, Goodings C, Voss RK, Kozyra EJ, Szvetnik A, Noellke P, Dworzak M, Starý J, Locatelli F, Masetti R, Schmugge M, De Moerloose B, Català-Temprano A, Kállay K, Turkiewicz D, Hasle H, Buechner J, Jahnukainen K, Ussowicz M, Polychronopoulou S, Smith OP, Fabri O, Barzilai S, de Haas V, Baumann I, Schwarz-Furlan S, European Working Group of MDS in Children (EWOG-MDS), Niewisch MR, Sauer MG, Burkhardt B, Lang P, Bader P, Beier R, Müller I, Albert MH, Meisel R, Schulz A, Cario G, Panda PK, Wehrle J, Hirabayashi S, Derecka M, Durruthy-Durruthy R, Göhring G, Yoshimi-Noellke A, Ku M, Lebrecht D, Erlacher M, Flotho C, Strahm B, Niemeyer CM and Wlodarski MW.

    Clinical evolution, genetic landscape and trajectories of clonal hematopoiesis in SAMD9/SAMD9L syndromes.

    NATURE MEDICINE . 27(10): 1806-1817. Nº de citas: 72

    [doi:10.1038/s41591-021-01511-6]

  • Sevilla J, Navarro S, Rio P, Sánchez-Domínguez R, Zubicaray J, Gálvez E, Merino E, Sebastián E, Azqueta C, Casado JA, Segovia JC, Alberquilla O, Bogliolo M, Román-Rodríguez FJ, Giménez Y, Larcher L, Salgado R, Pujol RM, Hladun R, Castillo A, Soulier J, Querol S, Fernández J, Schwartz J, García de Andoín N, López R, Català-Temprano A, Surralles J, Díaz-de-Heredia C and Bueren JA.

    Improved collection of hematopoietic stem cells and progenitors from Fanconi anemia patients for gene therapy purposes.

    Molecular Therapy-Methods & Clinical Development . 22: 66-75. Nº de citas: 7

    [doi:10.1016/j.omtm.2021.06.001]

  • Trifunov S, Paredes-Fuentes AJ, Badosa-Gallego MC, Codina-Bergadà A, Montoya C, Ruiz-Pesini E, Jou-Munoz C, Garrabou G, Grau-Junyent JM, Yubero-Siles D, Montero-Sanchez R, Muchart-Lopez J, Ortigoza-Escobar JD, O'Callaghan-Gordo M, Nascimento-Osorio A, Català-Temprano A, Garcia-Cazorla A, Jimenez-Mallebrera C and Artuch-Iriberri R.

    Circulating Cell-Free Mitochondrial DNA in Cerebrospinal Fluid as a Biomarker for Mitochondrial Diseases

    CLINICAL CHEMISTRY . 67(8): 1113-1121. Nº de citas: 6

    [doi:10.1093/clinchem/hvab091]

  • Ramírez MJ, Pujol R, Trujillo-Quintero JP, Minguillón J, Bogliolo M, Río P, Navarro S, Casado JA, Badell I, Carrasco E, Balmaña J, Català-Temprano A, Sevilla J, Beléndez C, Argilés B, López M, de Heredia CD, Rao G, Nicoletti E, Schwartz JD, Bueren JA and Surrallés J.

    Natural gene therapy by reverse mosaicism leads to improved hematology in Fanconi anemia patients.

    AMERICAN JOURNAL OF HEMATOLOGY . 96(8): 989-999. Nº de citas: 11

    [doi:10.1002/ajh.26234]

  • Navarro, S, Sevilla, J, Rio, P, Sanchez, R, Zubicaray, J, Galvez, E, Merino, E, Sebastian, E, Azqueta, C, Casado, JA, Segovia, JC, Alberquilla, O, Bogliolo, M, Roman-Rodriguez, FJ, Gimenez, Y, Larcher, L, Salgado, R, Pujol, RM, Haldun, R, Castillo, A, Soulier, J, Querol, S, Fernandez, J, Shcwartz, J, de Andoin, NG, Lopez, R, Català-Temprano A, Surralles, J, de Heredia, CD and Bueren, JA.

    Hematopoietic Stem Cell Collection for the Gene Therapy of Fanconi Anemia Patients

    MOLECULAR THERAPY . 29(4): 342-342.

  • Gálvez E, Vallespín E, Arias-Salgado EG, Sánchez-Valdepeñas C, Giménez Y, Navarro S, Río P, Bogliolo M, Pujol R, Peiró M, Nevado J, Zubicaray J, Sebastián E, Català-Temprano A, Beléndez C, Díaz de Heredia C, Galera A, Badell I, Madero L, Perona R, Sastre L, Surrallés J, Bueren J, Lapunzina P and Sevilla J.

    Next-generation Sequencing in Bone Marrow Failure Syndromes and Isolated Cytopenias: Experience of the Spanish Network on Bone Marrow Failure Syndromes.

    hemasphere . 5(4): . Nº de citas: 7

    [doi:10.1097/HS9.0000000000000539]

  • Vega-García N, Pérez-Jaume S, Esperanza-Cebollada E, Vicente-Garces C, Torrebadell-Burriel M, Jiménez-Velasco A, Ortega M, Llop M, Abad L, Vagace JM, Minguela A, Pratcorona M, Sánchez-Garcia J, García-Calderon CB, Gómez-Casares MT, Martín-Clavero E, Escudero A, Riñón M, Muñoz L, Velasco MR, García-Morín M, Català-Temprano A, Pascual A, Velasco P, Fernandez JM, Lassaletta A, Fuster JL, Badell I, Molinos-Quintana A, Molinés A, Guerra-Garcia P, Pérez-Martínez A, García-Abós M, Robles R, Pisa S, Adán R, Díaz de Heredia C, Dapena JL, Rives-Solà S, Ramirez M and Camós-Guijosa M.

    Measurable Residual Disease Assessed by Flow-Cytometry Is a Stable Prognostic Factor for Pediatric T-Cell Acute Lymphoblastic Leukemia in Consecutive SEHOP Protocols Whereas the Impact of Oncogenetics Depends on Treatment.

    Frontiers in pediatrics . 8: 614521-614521. Nº de citas: 3

    [doi:10.3389/fped.2020.614521]